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Home > Events > Next gen therapies for SJIA & MAS Conference Program (final)

Next gen therapies for SJIA & MAS Conference Program (final)

Rashmi Sinha | October 19, 2016 | 1 Comment

Here is the final program for the Next Gen therapies conference. Post a comment if you have any questions.

 OCTOBER 21st, FRIDAY
6.00pm:7.00pmDrinks & Hors D̥oeuvres
6.45pm:7.45pmWelcome & Keynote talk by Eric Hoffman
7.45pm:9.00pmDinner




OCTOBER 22nd, SATURDAY
7.30am:8.30amBreakfast
8.35am:8.45amIntro to conference (Rashmi)
8:45am:9:10amPatients panel: to understand patient perspective & need for next gen therapies
9:10am:9:15amSetting stage for next-gen drug discussion (Fabrizio De Benedetti)
Session 1: IL-18 and Interferon Gamma
9.20am:9.50amTargeting IL-18 (Scott Canna, Edward Behrens)
9.50am:10.20amTargeting Interferon Gamma (Alexei Grom, Fabrizio De Benedetti)
10.20am:10.40amPanel Discussion for Session 1
10.40am:11.00amBreak
Session 2: IL-1 & IL-17
11.00am:11.20amTargeting IL-1 (Peter Nigrovic)
11.20am:11.40amTargeting IL-17 Blocker (Pierre Miossec)
11.40am:12.00pmPanel discussion for Session 2
12.00pm:1.30pmLunch
Session 3: Jak STAT Pathway
1.30pm:1.50pmTargeting Jak-STAT Pathway I (Adriana Alameida de Jesus)
1.50pm:2.10pmTargeting Jak-STAT Pathway II (Kim Nichols - remote talk)
2.10pm:2.30pmPanel discussion for Session 3
2.30pm:3.00pmOpen Mic ̐ 5 mins each for other targets not discussed today
3.00pm:3.20pmBreak
Session 4: Getting Clinical Trials & Expanded Access
3.20pm:3.35pmNuts & Bolts of clinical trials in rare pediatric diseases: EMA perspective (Richard Vesely)
3.35pm:3.50pmNuts & Bolts of clinical trials in rare pediatric diseases: FDA perspective (FDA Rep)
3.50pm:4.05pmNuts & Bolts of clinical trials in rare pediatric diseases: Pharma perspective (Cristina de Min)
4.05pm:4.20pmExpanded Access Programs (FDA Rep)
4.20pm:5.30pmPanel Discussion for Clinical trials / Expanded Access (moderated by Alexei Grom)
6.30pm:7.00pmTake cabs to dinner (Meet at 6.30 in hotel foyer)
7.00pm:9.00pmDinner




OCTOBER 23rd SUNDAY
7.30am:8.30amBreakfast
7.30am:8.30amMesenchymal Stem Cell Focus Groups (Patients & Nora Singer)
8.30am:9.20amOpen time (for ad-hoc discussions)
Session 5: Stem Cell Transplantation
9.20am:9.40amOverview & Autologous transplantation in SJIA (Nico Wulffraat & Lucy Wedderburn - remote)
9.40am:10.00amAllogeneic Stem Cell Transplantation in SJIA (Paul Veys - remote talk)
10.00am:10.20amBMT in HLH (Rebecca Marsh)
10.20am:10.40amBreak
10.40am:11.40amPanel Discussion of Stem Cell Transplantation (moderated by Nico Wulffraat)
Session 6: Mesenchymal Stem Cells
11.40am:11.55amMSCs in SJIA (Nico Wulffraat)
11.55am:12.10pmMSCs in SJIA: Plan for clinical trials (Nora Singer)
12.10pm:12.30pmPanel discussion of MSCs
12.30pm:2.00pmLunch
2.00pm-3.00pmSession 7: Reflections and conference wrap up

Trackbacks

  1. Vamorolone: A steroid replacement with fewer side effects - Systemic JIA Foundation says:
    January 19, 2017 at 9:42 pm

    […] a researcher in another childhood disease (Duchenne Muscular Dystrophy), gave the keynote at our next-gen SJIA treatments conference in October. He is leading an effort at Reveragen to bring a steroid replacement called Vamorolone […]

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